Catabasis Pharmaceuticals, Inc. CATB, a clinical-stage biopharmaceutical company, today announced that it will present data from Part A and Part B of the MoveDMD trial of edasalonexent (CAT-1004) for the treatment of Duchenne muscular dystrophy (DMD) at the American Academy of Neurology 69th Annual Meeting to be held April 22 – 28, 2017, in Boston, MA, at the Boston Convention and Exhibition Center.
Joanne Donovan, M.D., Ph.D., Chief Medical Officer of Catabasis, will present the poster "MoveDMD Results: Effects of Edasalonexent, an NF-kB Inhibitor, in 4 to 7 Year Old Patients with Duchenne Muscular Dystrophy" during Poster Session 3 on Tuesday, April 25, 2017 from 5:30pm – 7:00pm ET.
About Edasalonexent (CAT-1004)
Edasalonexent (CAT-1004) is
an investigational oral small molecule that is being developed as a
potential disease-modifying therapy for all patients affected by DMD,
regardless of their underlying mutation. Edasalonexent inhibits NF-kB, a
protein that is activated in DMD and drives inflammation and fibrosis,
muscle degeneration and suppresses muscle regeneration. We are currently
conducting the MoveDMD® trial, a three-part clinical trial
investigating the safety and efficacy of edasalonexent in boys ages 4 –
7 affected with DMD (any confirmed mutation). The third part of the
trial, an open-label extension with edasalonexent, is ongoing. The FDA
has granted orphan drug, fast track and rare pediatric disease
designations and the European Commission has granted orphan medicinal
product designation to edasalonexent for the treatment of DMD. For a
summary of clinical results reported to-date, please visit www.catabasis.com.
About Catabasis
At Catabasis Pharmaceuticals, our mission is
to bring hope and life-changing therapies to patients and their
families. Our SMART (Safely Metabolized And Rationally Targeted) linker
drug discovery platform enables us to engineer molecules that
simultaneously modulate multiple targets in a disease. We are applying
our SMART linker platform to build an internal pipeline of product
candidates for rare diseases and plan to pursue partnerships to develop
additional product candidates. For more information on the Company's
drug discovery platform and pipeline of drug candidates, please visit www.catabasis.com.
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