| Sep 14, 2026 | 1:00 PM | — | H.c. Wainwright 28th Annual Global Investor Conference | Corporate Conference Presentation | 2 | New York, NY | | Source |
| Sep 10, 2026 | 3:00 PM | — | Citi's 2026 Biopharma Back To School Conference | Corporate Conference Presentation | 2 | New York, NY | | Source |
| Sep 9, 2026 | 3:55 PM | — | 2026 Cantor Global Healthcare Conference | Corporate Conference Presentation | 2 | New York, NY | | Source |
| Jun 8, 2026 | 4:00 PM | — | Goldman Sachs 47th Annual Global Healthcare Conference | Corporate Conference Presentation | 2 | Miami, FL | | Source |
| Jun 3, 2026 | 7:35 AM | — | Jefferies Global Healthcare Conference | Corporate Conference Presentation | 2 | New York | — | Source |
| May 11, 2026 | 8:00 AM | May 15, 2026 | 29th Annual Meeting Of The American Society Of Gene & Cell Therapy (asgct) | Corporate Conference Presentation | 2 | Boston, MA. | — | Source |
| Apr 14, 2026 | 2:15 PM | — | 25th Annual Needham Virtual Healthcare Conference | Corporate Conference Presentation | 2 | Virtual | | Source |
| Mar 11, 2026 | 1:00 PM | — | Muscular Dystrophy Association (mda) Clinical & Scientific Conference | Corporate Conference Presentation | 2 | — | — | Source |
| Feb 12, 2026 | 10:30 AM | — | Guggenheim Emerging Outlook: Biotech Summit 2026 | Summit | 2 | New York | — | — |
| Jan 13, 2026 | 8:15 PM | — | 44th Annual J.p. Morgan Healthcare Conference | Corporate Conference Presentation | 2 | San Francisco, California | | Source |
| Dec 2, 2025 | 11:30 AM | — | Piper Sandler 37th Annual Healthcare Conference | Corporate Conference Presentation | 2 | New York | | Source |
| Nov 18, 2025 | 6:00 AM | — | Jefferies London Global Healthcare Conference | Corporate Conference Presentation | 2 | London, United Kingdom | | Source |
| Sep 26, 2025 | 8:00 AM | Sep 28, 2025 | 26th Annual Scientific Meeting Of Neuromuscular Study Group (nmsg) | Summit | 2 | Stresa, Italy | — | Source |
| May 7, 2025 | 12:30 PM | — | Citizens Life Sciences Conference | Corporate Conference Presentation | 1 | New York | | Source |
| Apr 17, 2025 | 8:00 AM | — | Piper Sandler Spring Biopharma Symposium | Summit | 1 | Boston, MA | — | Source |
| Apr 10, 2025 | 2:15 PM | — | Needham's 24th Annual Healthcare Conference | Corporate Conference Presentation | 1 | Virtual | | Source |
| Mar 13, 2025 | 9:30 AM | — | Barclays 27th Annual Global Healthcare Conference | Corporate Conference Presentation | 1 | Miami, Florida | | Source |
| Mar 12, 2025 | 9:20 AM | — | Leerink Global Healthcare Conference | Corporate Conference Presentation | 1 | Miami, Florida | | Source |
| Jan 15, 2025 | 6:45 PM | — | J.p. Morgan 43rd Annual Healthcare Conference | Corporate Conference Presentation | 1 | San Francisco, California | | Source |
| Dec 5, 2024 | 9:30 AM | — | Piper Sandler's 36th Annual Healthcare Conference | Corporate Conference Presentation | 1 | New York | | Source |
| Dec 4, 2024 | 1:00 PM | — | Citi's 2024 Global Healthcare Conference | Corporate Conference Presentation | 1 | Miami, FL | | Source |
| Nov 20, 2024 | 8:30 AM | — | Jefferies London Healthcare Conference | Corporate Conference Presentation | 1 | London | | Source |
| Nov 7, 2024 | 1:45 PM | — | Truist Securities Biopharma Symposium | Summit | 1 | New York | — | Source |
| Sep 30, 2024 | 11:00 AM | — | Chardan's 8th Annual Genetic Medicines Conference | Corporate Conference Presentation | 1 | New York | | Source |
| Sep 18, 2024 | 10:20 AM | — | Cantor Fitzgerald Global Healthcare Conference | Corporate Conference Presentation | 1 | New York | | Source |
| Sep 11, 2024 | 12:50 PM | — | Baird's 2024 Global Healthcare Conference | Corporate Conference Presentation | 1 | New York | — | Source |
| Sep 10, 2024 | 9:30 AM | — | H.c. Wainwright 26th Annual Global Investment Conference | Corporate Conference Presentation | 1 | New York | | Source |
| Apr 2, 2024 | 8:15 AM | — | Virtual Muscular Dystrophy Symposium | — | — | — | | Source |