| Sep 25, 2026 | 8:00 AM | Sep 27, 2026 | 27th Annual Neuromuscular Study Group (nmsg) Scientific Meeting | Corporate Conference Presentation | 3 | San Antonio, TX. | — | Source |
| Sep 15, 2026 | 10:50 AM | — | Baird 2026 Global Healthcare Conference | Corporate Conference Presentation | 3 | New York, NY | | Source |
| Sep 14, 2026 | 9:15 AM | — | Morgan Stanley 24th Annual Global Healthcare Conference | Corporate Conference Presentation | 3 | New York, NY | | Source |
| Sep 11, 2026 | 10:20 AM | — | 2026 Cantor Global Healthcare Conference | Corporate Conference Presentation | 3 | New York,NY | | Source |
| Jun 9, 2026 | 8:00 AM | — | Goldman Sachs 47th Annual Global Healthcare Conference | Corporate Conference Presentation | 3 | Miami, FL | — | Source |
| Jun 3, 2026 | 9:55 AM | — | Jefferies Global Healthcare Conference, | Corporate Conference Presentation | 3 | New York, NY | — | Source |
| May 20, 2026 | 11:00 AM | — | Rbc Capital Markets Global Healthcare Conference, | Corporate Conference Presentation | 3 | New York, NY | — | Source |
| May 11, 2026 | 8:00 AM | May 15, 2026 | American Society Of Gene & Cell Therapy (asgct) 2026 Annual Meeting | Corporate Conference Presentation | 3 | Boston, MA. | — | Source |
| Apr 13, 2026 | 8:00 AM | Apr 16, 2026 | Academy Of Managed Care Pharmacy (amcp) Conference | Corporate Conference Presentation | 3 | Nashville, TN. | — | Source |
| Mar 17, 2026 | 4:00 PM | — | Stifel 2026 Virtual Cns Forum, | Summit | 3 | — | — | Source |
| Mar 10, 2026 | 8:00 AM | Mar 11, 2026 | 2026 Jefferies Biotech On The Beach Summit, | Summit | 3 | Miami, Florida | — | Source |
| Mar 4, 2026 | 11:50 AM | — | Td Cowen 46th Annual Healthcare Conference | Corporate Conference Presentation | 3 | Boston, MA | | Source |
| Jan 14, 2026 | 8:15 PM | — | 44th Annual J.p. Morgan Healthcare Conference | Corporate Conference Presentation | 3 | San Francisco, California | | Source |
| Sep 8, 2025 | 9:15 AM | — | Morgan Stanley 23rd Annual Global Healthcare Conference | Corporate Conference Presentation | 2 | New York | | Source |
| Sep 5, 2025 | 9:45 AM | — | Cantor Global Healthcare Conference | Corporate Conference Presentation | 2 | New York | | Source |
| Mar 18, 2025 | 4:00 PM | — | Stifel 2025 Virtual Cns Forum | Summit | 3 | Virtual | | Source |
| Mar 18, 2025 | 1:00 PM | — | Muscular Dystrophy Association (mda) Clinical & Scientific Conference | Corporate Conference Presentation | 3 | — | — | Source |
| Feb 11, 2025 | 4:00 PM | — | Oppenheimer 35th Annual Healthcare Life Sciences Conference | Corporate Conference Presentation | 3 | Virtual | | Source |
| Jan 15, 2025 | 1:30 PM | — | J.p. Morgan 43rd Annual Healthcare Conference | Corporate Conference Presentation | 3 | San Francisco, California | — | Source |
| Jan 10, 2025 | 8:00 AM | — | Investor Conference Call | Investor Conference | 3 | — | | Source |
| Oct 11, 2024 | 9:45 AM | — | 29th Annual Congress Of The World Muscle Society 2024 Congress (wms 2024) | Summit | 3 | Prague, Czechia | — | Source |
| Sep 30, 2024 | 2:00 PM | — | Chardan's 8th Annual Genetic Medicines Conference | Corporate Conference Presentation | 3 | New York | | Source |
| Sep 5, 2024 | 4:05 PM | — | Morgan Stanley 22nd Annual Global Healthcare Conference | Corporate Conference Presentation | 3 | New York | | Source |
| Jun 6, 2024 | 3:00 PM | — | Jefferies Global Healthcare Conference | Corporate Conference Presentation | — | New York | | Source |
| Apr 2, 2024 | 9:50 AM | — | Cantor Virtual Muscular Dystrophy Symposium | Corporate Conference Presentation | — | Virtual | | Source |
| Apr 2, 2024 | 8:00 AM | Apr 3, 2024 | Cantor Virtual Muscular Dystrophy Symposium | Corporate Conference Presentation | — | Virtual | | — |