Market Overview

Niemann-Pick Disease | A Pipeline Analysis Report 2018 | Technavio


Technavio has announced their latest pipeline analysis report on the Niemann-Pick
disease market
. The report includes a detailed analysis of the
pipeline molecules under investigation within the defined data
collection period to treat Niemann-Pick disease.

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Technavio has published a new report on the drug development pipeline for Niemann-pick disease, incl ...

Technavio has published a new report on the drug development pipeline for Niemann-pick disease, including a detailed study of the pipeline molecules. (Graphic: Business Wire)

This report by Technavio
presents a detailed analysis of the market, including regulatory
framework, drug development strategies, recruitment strategies, and key
companies that are expected to play an essential role in the growth of
the market in the future.

This report is available at a USD 1,000 discount for a limited time
market snapshot before purchasing

Niemann-Pick disease: Market overview

Niemann-Pick disease is a rare, inherited disease that affects the
body's ability to metabolize cholesterol and lipids within cells.
Niemann-Pick disease can affect the brain, nerves, liver, spleen, bone
marrow, and lungs (in severe cases). People with Niemann-Pick disease
experience symptoms related to the progressive function loss of the
nerves, the brain, and other organs.

According to a senior market research analyst at Technavio, "Niemann-Pick
disease can occur at any age, but it mainly affects children. The
disease has no known cure and is sometimes fatal. According to the US
National Library of Medicines, Niemann-Pick disease type A and B are
estimated to affect 1 in 250,000 individuals. Niemann-Pick disease type
A occurs more frequently among individuals of Ashkenazi, an Eastern and
Central European Jewish descent, than in the general population."

Niemann-Pick disease: Segmentation analysis

This pipeline analysis report segments the Niemann-Pick disease market
based on therapies employed (monotherapy), RoA (oral, intravenous, and
intrathecal), therapeutic modality (small molecule, oligosaccharide,
recombinant enzyme, and amino acid), targets (cholesterol,
sphingomyelin, human ASM, PKC epsilon, HSP 70, and histone deacetylase),
MoA (cholesterol modulator, sphingomyelin inhibitor, ASM replacement,
PKC epsilon inhibitor, HSP 70 inducer, and HDAC inhibitor), geographical
segmentation (US, UK, France, Italy, Germany, and others) and
recruitment status (active, not recruiting, completed, recruiting, and
enrolling by invitation). It provides an in-depth analysis of the
prominent factors influencing the market, including drivers,
opportunities, trends, and industry-specific challenges.

Based on therapeutic modality, around 42% of the molecules that are
being investigated for the treatment of Niemann-Pick disease are small

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Some of the key topics covered in the report include:

Scope of the Report

Regulatory Framework

Drug Development Landscape

  • Drugs under development
  • Indications coverage

Drug Development Strategies

  • Therapies employed
  • RoA
  • Therapeutic modality
  • Geographical coverage

Recruitment Strategies

  • Recruitment status
  • Gender
  • Age

Key Companies

  • Type of players
  • Company overview

Discontinued or Dormant Molecules

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