Orphan Drug Designation Recent News
Allogene's BCMA-Targeted Therapy Gets US Orphan Drug Tag For Multiple Myeloma
C4 Therapeutics Multiple Myeloma Candidate Scores FDA Orphan Drug Tag
Lantern Pharma Secures FDA Orphan Drug Tag For Pancreatic Cancer Candidate
Akouos' Hearing Loss Gene Therapy Poised To Receive Orphan Drug Tag In Europe
Aldeyra Secures US Orphan Drug Tag For Its Retinitis Pigmentosa Candidate
Relief Therapeutics' Lead Candidate Gets US Orphan Drug Tag In Sarcoidosis
Aldeyra Stock Trading Higher On FDA Orphan Drug Tag For Primary Vitreoretinal Lymphoma Candidate
Soleno Stock Shoots Higher as Diazoxide Choline Gets US Orphan Drug Tag for Glycogen Storage Disease
Seelos's Amyotrophic Lateral Sclerosis Candidate, SLS-005 An Orphan Drug In Europe
Moleculin Biotech Stock Is Trading Higher After WP1066 Scores Rare Pediatric Disease Tag For Type Of Brain Tumor
Why Surface Oncology Shares Spiked 19% Today
BridgeBio Pharma Gets First FDA-Approval For Rare Genetic Metabolic Disorder
AIM ImmunoTech Gets Orphan Drug Tag For Ampligen In Pancreatic Cancer
Cerecor's CERC-803 Nabs US Orphan Drug Tag In Rare Immunodeficiency Disorder
Shares Of Pluristem Therapeutics Surging Following Receipt Of Orphan Drug Designation
Why Shares of Ignyta Are Trading Higher